meili 发表于 2022-10-18 21:41:39

首个白血病治疗基因疗法在美获批

<p>美国监管机构8月30日批准一种基于改造患者自身免疫细胞的疗法治疗白血病,这是第一种在美国获得批准的基因疗法。专家认为,这开辟了癌症治疗的新篇章。</p><p><span word="US">US</span> <span word="regulators">regulators</span> <span word="on">on</span> <span word="Wednesday">Wednesday</span> <span word="approved">approved</span> <span word="the">the</span> <span word="first">first</span> <span word="gene">gene</span> <span word="therapy">therapy</span> <span word="against">against</span> <span word="cancer">cancer</span> - <span word="a">a</span> <span word="treatment">treatment</span> <span word="that">that</span> <span word="uses">uses</span> <span word="a">a</span> <span word="patient">patient</span>'<span word="s">s</span> <span word="own">own</span> <span word="immune">immune</span> <span word="cells">cells</span> <span word="to">to</span> <span word="fight">fight</span> <span word="leukemia">leukemia</span> - <span word="opening">opening</span> <span word="a">a</span> <span word="new">new</span> <span word="era">era</span> <span word="in">in</span> <span word="the">the</span> <span word="fight">fight</span> <span word="against">against</span> <span word="one">one</span> <span word="of">of</span> <span word="the">the</span> <span word="world">world</span>'<span word="s">s</span> <span word="top">top</span> <span word="killers">killers</span>.</p><p>美国监管机构于8月30日批准了首个对抗癌症的基因治疗手段——使用患者的免疫细胞对抗白血病。白血病是世界上致死率最高的疾病之一,该治疗手段开启了对抗白血病的新纪元。</p><p><span word="The">The</span> <span word="treatment">treatment</span> <span word="is">is</span> <span word="made">made</span> <span word="by">by</span> <span word="Novartis">Novartis</span> <span word="and">and</span> <span word="is">is</span> <span word="called">called</span> <span word="Kymriah">Kymriah</span>.</p><p>该疗法由诺华公司研发,并被命名为<span word="Kymriah">Kymriah</span>。</p><p><span word="This">This</span> <span word="type">type</span> <span word="of">of</span> <span word="anti">anti</span>-<span word="cancer">cancer</span> <span word="immunotherapy">immunotherapy</span>, <span word="known">known</span> <span word="as">as</span> <span word="a">a</span> <span word="CAR">CAR</span>-<span word="T">T</span> <span word="cell">cell</span> <span word="therapy">therapy</span>, <span word="was">was</span> <span word="known">known</span> <span word="by">by</span> <span word="CTL">CTL</span>019 <span word="until">until</span> <span word="now">now</span>.</p><p>这种对抗癌症的免疫疗法也被称作<span word="CAR">CAR</span>-<span word="T">T</span>细胞疗法,并因<span word="CTL">CTL</span>019疗法(一种<span word="CAR">CAR</span>-<span word="T">T</span>细胞疗法)被人们熟知。</p><p>"<span word="This">This</span> <span word="marks">marks</span> <span word="the">the</span> <span word="first">first</span>-<span word="ever">ever</span> <span word="CAR">CAR</span>-<span word="T">T</span> <span word="cell">cell</span> <span word="therapy">therapy</span> <span word="to">to</span> <span word="be">be</span> <span word="approved">approved</span> <span word="anywhere">anywhere</span> <span word="in">in</span> <span word="the">the</span> <span word="world">world</span>," <span word="Novartis">Novartis</span> <span word="CEO">CEO</span> <span word="Joseph">Joseph</span> <span word="Jimenez">Jimenez</span> <span word="told">told</span> <span word="reporters">reporters</span> <span word="on">on</span> <span word="a">a</span> <span word="conference">conference</span> <span word="call">call</span>.</p><p>诺华<span word="CEO">CEO</span>江慕忠在一次电话会议上对记者说:“这是全球首次允许使用<span word="CAR">CAR</span>-<span word="T">T</span>细胞疗法。”</p><p>"<span word="It">It</span> <span word="uses">uses</span> <span word="a">a</span> <span word="new">new</span> <span word="approach">approach</span> <span word="that">that</span> <span word="is">is</span> <span word="wholly">wholly</span> <span word="personalized">personalized</span> <span word="by">by</span> <span word="using">using</span> <span word="a">a</span> <span word="patient">patient</span>'<span word="s">s</span> <span word="own">own</span> <span word="T">T</span>-<span word="cells">cells</span>."</p><p>“这种新疗法使用患者自己的<span word="T">T</span>细胞,是完全个性化的。”</p>
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