meili 发表于 2022-10-18 21:25:02

科学家将要用基因编辑技术治疗先天失明

<p><span word="CRISPR">CRISPR</span> <span word="is">is</span> <span word="coming">coming</span> <span word="for">for</span> <span word="your">your</span> <span word="body">body</span>. <span word="While">While</span> <span word="that">that</span> <span word="may">may</span> <span word="sound">sound</span> <span word="like">like</span> <span word="the">the</span> <span word="tagline">tagline</span> <span word="of">of</span> <span word="a">a</span> <span word="horror">horror</span> <span word="film">film</span>, <span word="it">it</span>’<span word="s">s</span> <span word="potentially">potentially</span> <span word="the">the</span> <span word="future">future</span> <span word="of">of</span> <span word="medicine">medicine</span>, <span word="as">as</span> <span word="the">the</span> <span word="gene">gene</span>-<span word="editing">editing</span> <span word="technique">technique</span> <span word="is">is</span> <span word="about">about</span> <span word="to">to</span> <span word="be">be</span> <span word="used">used</span> <span word="for">for</span> <span word="the">the</span> <span word="first">first</span> <span word="time">time</span> <span word="inside">inside</span> <span word="the">the</span> <span word="bodies">bodies</span> <span word="of">of</span> <span word="presumably">presumably</span> <span word="willing">willing</span> <span word="patients">patients</span>.</p><p><span word="CRISPR">CRISPR</span>(成簇规律间隔的短回文重复序列,近年来被认为是原核生物适应性免疫结构)即将进入你的身体。虽然这听上去可能有点像一部恐怖电影的口号,但这也许是医药研究的未来,因为基因编辑技术将首次被用于想必是自愿接受的病人的身体上。</p><p><span word="The">The</span> <span word="first">first</span> <span word="trial">trial</span> <span word="could">could</span> <span word="be">be</span> <span word="an">an</span> <span word="impressive">impressive</span> <span word="feat">feat</span> <span word="of">of</span> <span word="modern">modern</span> <span word="medicine">medicine</span>: <span word="Scientists">Scientists</span> <span word="hope">hope</span> <span word="to">to</span> <span word="use">use</span> <span word="CRISPR">CRISPR</span>’<span word="s">s</span> <span word="gene">gene</span>-<span word="editing">editing</span> <span word="magic">magic</span> <span word="to">to</span> <span word="restore">restore</span> <span word="sight">sight</span> <span word="to">to</span> <span word="people">people</span> <span word="with">with</span> <span word="an">an</span> <span word="inherited">inherited</span> <span word="form">form</span> <span word="of">of</span> <span word="blindness">blindness</span> <span word="called">called</span> <span word="Leber">Leber</span> <span word="congenital">congenital</span> <span word="amaurosis">amaurosis</span>.</p><p>这次尝试可能是现代医药的一次令人印象深刻的壮举:科学家希望利用<span word="CRISPR">CRISPR</span>基因编辑的魔力来恢复遗传性失明(又被称为莱伯士先天性黑朦)的人的视力。</p><p><span word="It">It</span>’<span word="s">s</span> <span word="the">the</span> <span word="most">most</span> <span word="common">common</span> <span word="cause">cause</span> <span word="of">of</span> <span word="inherited">inherited</span> <span word="childhood">childhood</span> <span word="blindness">blindness</span>, <span word="occurring">occurring</span> <span word="in">in</span> <span word="about">about</span> 2 <span word="to">to</span> 3 <span word="of">of</span> <span word="every">every</span> 100,000 <span word="births">births</span>, <span word="according">according</span> <span word="to">to</span> <span word="the">the</span> <span word="AP">AP</span>.</p><p>据美国联合通讯社报道,这是儿童遗传性失明最常见的原因,每十万个新生儿中就会有2~3个人患有遗传性失明。</p><p><span word="People">People</span> <span word="with">with</span> <span word="the">the</span> <span word="disease">disease</span> <span word="lack">lack</span> <span word="just">just</span> <span word="one">one</span> <span word="gene">gene</span>, <span word="the">the</span> <span word="gene">gene</span> <span word="that">that</span> <span word="converts">converts</span> <span word="light">light</span> <span word="into">into</span> <span word="signals">signals</span> <span word="to">to</span> <span word="the">the</span> <span word="brain">brain</span> <span word="and">and</span> <span word="lets">lets</span> <span word="the">the</span> <span word="eyes">eyes</span> <span word="do">do</span> <span word="their">their</span> <span word="job">job</span>.</p>
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